Repurposing drugs for rare diseases involves using existing medications for new therapeutic purposes. This approach saves time, reduces development costs, and accelerates treatment availability. It offers hope for patients with orphan diseases, where research is limited due to low prevalence and profitability, making drug repurposing a promising pharmaceutical strategy.
1 Like
This is impressive, can you give me some examples of which drug was repurposed?
Thalidomide for multiple myeloma
1 Like
Drug repurposing can provide several advantages like it’s safety and toxicity data can be taken into account directly and this reduces the costs highly during a clinical trial as compared to a completely new drug discovery process. But, IP (intellectual property) rights can emerge here. The mechanism through which this drug can act now for a new diseased condition also should be outlined clearly and it’s efficacy should be evaluated properly.
1 Like